Pipeline

Pipeline.

Our systematic approach to therapeutics discovery starts with the development of a patient biobank and validation of a disease-specific, in vitro deep phenotype, which serve as the inputs into our scaled drug discovery engine.

Each of our disease programs, from discovery through clinical trials, is continually informed by this rigorous scientific foundation and therefore has a greater chance of truly moving the needle in curing brain disease.

Rett Syndrome

Rett Syndrome

Rett syndrome is a rare genetic neurological disorder that occurs almost exclusively in girls and leads to severe impairments in their ability to speak, walk, eat, and even breathe easily.

Alzheimer's Disease

Alzheimer's Disease

Alzheimer’s is a type of dementia that affects thinking, behavior and memory. Eventually, these symptoms grow severe enough to impact daily tasks.

Schizophrenia

Schizophrenia

Schizophrenia is a serious mental illness that interferes with a person’s ability to think clearly, manage emotions, make decisions and relate to others.